News New Tool to Help With Virtual Research and Care Management for Duchenne Patients

News Trial Testing WVE-210201 in DMD Selected for FDA Pilot Program

News Sarepta and Aldevron Partnering on Gene Therapy Program for DMD and LGMD

columns, You, Me and MD - a Column by Leah Leilani I’ve Learned How to Deal with Judgment About My Disease

News DMD Hub Works to Connect Patients with Clinical Trials, Promote Study Sites Across UK

News PPMD Awards $329K to Researchers Looking to Better Understand Promising Duchenne Therapies

News Phase 3 Trial of Edasalonexent in DMD Now Enrolling Across US, Global Sites to Follow

News Capricor Places Hold on Phase 2 Trial of Cell Therapy After Patient Has Allergic Reaction

News Myonexus’ MYO-102 Earns FDA’s Orphan Drug Status for LGMD 2D

News Project Hercules Enlists Industry’s Help to Make Duchenne Therapies Affordable

News Top 10 Muscular Dystrophy Articles of 2018

News Rising Healthcare Costs Strain EU Budgets Even as New Therapies Flourish

News PPMD Webinar Takes In-depth Look at MD Cardiac Disease and Recent Research Efforts

News Neurologist Urges Greater Focus on Brain Issues in Duchenne

columns, You, Me and MD - a Column by Leah Leilani Here’s How I Decorated My Wheelchair This Christmas

News Potential DMD Therapy WVE-210201 Shows Positive Phase 1 Safety Results

News Budding Journalist Hawken Miller Offers Advice on Living With Duchenne

News Coping with Duchenne: Parents Swap Stories at ‘Futures’ Conference

columns, You, Me and MD - a Column by Leah Leilani Seasonal Cooking with Mito

News UVA Children’s Hospital Recognized for Expert Duchenne Care by Parent Project MD

News Muscular Dystrophy UK Partners to Make Toilets on England’s Roadways More Accessible to All

News Neurologist Brenda Wong Heads New Specialized Duchenne Clinic at UMass

columns, You, Me and MD - a Column by Leah Leilani Small Ways to Get in the Holiday Spirit

News Taiho’s TAS-205 May Represent New Therapy Option for DMD, Phase 1 Data Shows

News West Virginia Mom of Duchenne Boy Struggles to Make Ends Meet

News Controlling BMI and Blood Pressure Might Slow Heart Damage in DMD Patients, Study Suggests

News Diabetes Treatment, Metformin, Seen to Aid Muscle Function and Overall Health of Mice with Congenital Muscular Dystrophy

News Duchenne UK Awards £655K to Evox Therapeutics to Develop New Way of Gene Therapy Delivery

columns, You, Me and MD - a Column by Leah Leilani My Introduction to Medical Marijuana

News US Midterm Election Results Bode Well for Healthcare Policy, Rare Disease Advocates Say

News Catabasis, UT Southwestern Collaborate to Explore Effect of Edasalonexent on Heart Function in Muscular Dystrophies

News CureDuchenne and Avidity Biosciences Hosting Webinar Friday on Potential DMD Therapies

News Extracellular RNAs in Urine May Work as Biomarker for Duchenne and Myotonic Dystrophy Patients

News Phase 3 Trial of Edasalonexent in Boys with DMD and Any Mutation Enrolling in US, Catabasis Reports

News Jiffy Lube’s ‘Muscle Up!’ Campaign Raises $600K for Muscular Dystrophy Association

News Children’s National Health System Named PPMD Certified Duchenne Care Center

News Pathway Key to Muscle Regeneration Doesn’t Work as It Should in Duchenne, Study Finds

News Capricor’s Vesicle-based Therapy Holds Promise to Treat DMD, Preclinical Data Suggests

News Cure Duchenne Kicks Off Inaugural ‘Pinkies Up to CureDuchenne’ Fundraising Campaign

columns, You, Me and MD - a Column by Leah Leilani Here’s How I Host Parties While Still Caring for My Body

News #NORDSummit – Major Issues on Table for Rare Disease Patients in US as Midterm Elections Approach

News Muscle Biopsy Aids Diagnosis, Treatment of Muscular Dystrophy in Children, Study Suggests

News MDA New York Muscle Team Readies for 22nd Annual Gala

columns, You, Me and MD - a Column by Leah Leilani Making Medication Compliance Easier

News Caregiving in DMD Has Significant Overall Impact on Everyday Life, Health, Review Shows

News Australian Research Team Awarded Nearly $490K to Study Taurine as a Potential DMD Treatment

News CureDuchenne and ZappRx Partner to Help DMD Patients More Easily Access Medications

News CureDuchenne Partners with Baebies to Advance ‘Easy’ Newborn Screening Test for DMD

columns, You, Me and MD - a Column by Leah Leilani Wheelchair-accessible Halloween Happenings

News GsMTx4 a Promising ‘Out-of-the-Box’ Therapy for Advanced DMD, Mouse Study Shows

News Sarepta’s Gene Therapy Improves Muscle Function in 4 Boys with DMD, Phase 1/2 Trial Shows

News Advocacy Groups, Doctors Question Rising Prices of Rare Disease Treatments

News CureDuchenne Hosting ‘Futures’ Conference Nov. 3-4 in Boston

columns, You, Me and MD - a Column by Leah Leilani The Simple Act of Opening a Door for Someone

News Miles for Matthew Fundraiser Marks 10-Year Milestone in Fight Against DMD

News Long-term Use of Steroids Linked to Weight Gain in Nonambulatory DMD Males, Study Reveals

News MuscleMap Automated Dystrophin Analysis Tool Can Help in DMD Assessment, Study Suggests

News Phase 3 Trial of Edasalonexent in Treating DMD Opening Soon, Catabasis Says

News FDA Lifts Hold on Sarepta’s Phase 1/2 Trial on Gene Therapy for DMD

columns, You, Me and MD - a Column by Leah Leilani Things to Keep in Mind When Choosing a Wheelchair

News College Football Coaches Joining Fight Against DMD During Annual Coach To Cure MD Event

News #NORDSummit – More Than 700 Expected to Attend Oct. 15-16 Rare Disease Summit in Washington

News Nonprofit Coalition to Cure Calpain 3 Funds 2 Gene Therapy Research Projects for LGMD2A

News Potential DMD Therapy Vamorolone Shows Positive Effects in Phase 2a Trial, Study Reports

columns, You, Me and MD - a Column by Leah Leilani A Girl’s Best Friend: Thoughts on Mobility Assistance Dogs

News Obsessive Compulsive Disorders Evident in Duchenne Patients and in Need of Treatment, Study Says

News Gene Editing Restored Dystrophin Levels in Dog Model of Duchenne MD, Study Reports

News STRIVE Awards Recognize Efforts of Duchenne MD Patient Groups Worldwide

columns, You, Me and MD - a Column by Leah Leilani Listening and Surrendering to My Body Isn’t Always Easy

News Numotion, Sing Me a Story Partner to Help Children with Neuromuscular Diseases Turn Life Stories to Songs

News Pfizer Stops Phase 2 Clinical Studies of Domagrozumab in DMD Boys

News PPMD and Jett Foundation Among Groups Gearing Up for Sept. 7, World Duchenne Awareness Day

columns, You, Me and MD - a Column by Leah Leilani Finding Doctors Who Understand Your Disease

News FSH Society Holding ‘Walk & Roll’ Event in Pacific Northwest to Raise Funds, Awareness for FSHD

News Service Dogs Just One Way Israel’s ‘Little Steps’ Assists Duchenne, Becker Patients

News MDA Awards $9.9M to 34 Projects Targeting Neuromuscular Diseases

News Canadian Collaboration Gives Funding Boost to Duchenne MD Research

News Long-term, Daily Glucocorticoid Use Raises Risk of Spinal Fractures in Duchenne Boys, U.K. Study Suggests

News Michigan Mom Who Lost One Son to Duchenne Works to Give Fresh Hope to the Other

News WVE-210201 Receives FDA Orphan Drug, Rare Pediatric Disease Designations for DMD

columns, You, Me and MD - a Column by Leah Leilani Seeing Both Sides of the Plastic Straw Controversy

News Jiffy Lube, MDA Join Forces for 7th Annual MUSCLE UP! Campaign

News 2 Nonprofits Join Forces to Help Duchenne Patients Fight Insurance Denials

News First Patient Enrolled in Phase 2 Trial of MNK-1411, Mallinckrodt’s Investigational Therapy for DMD

News Arizona Woman with Duchenne is a Rarity Among the Rare

columns, You, Me and MD - a Column by Leah Leilani How Lyrica Has Affected My Relationship with Food

News $700,000 MDA Grant to Help Establish LGMD Clinical Research Network

News New Online Resource, DuchenneXchange, and Its Offerings Explained in Aug. 7 Webinar

News Family’s Quest for ‘Overlooked’ Duchenne Treatments Leads to Breast Cancer Medicine Tamoxifen

News FDA Places Hold on Phase 1/2 Trial of Sarepta’s Gene Therapy for DMD

News Consortium.AI to Advance New Treatments for Duchenne Using Artificial Intelligence

News MDA Hellas Gives Greek SMA, Duchenne Patients Reason to Hope

News In Greece, One Family’s Struggle with Duchenne

columns, You, Me and MD - a Column by Leah Leilani Why I Identify with Being Chronically Ill, Not Disabled

News Raxone Delays Assisted Ventilation in DMD Patients by 3 Years, Phase 3 Trial Results Show

News Axovant Enters Global Licensing Deal with Benitec for Investigational AXO-AAV-OPMD Program to Treat OPMD

News Acceleron’s ACE-083 Earns Orphan Drug Status for Facioscapulohumeral MD

News #PPMD2018 – Mexico Lags in Degree and Quality of Duchenne Care, Advocacy Groups Say

columns, You, Me and MD - a Column by Leah Leilani Treat Your Mental Health Before It Becomes Too Much to Bear

News #PPMD2018 — ‘Mitchell’s Journey’ Supports Duchenne Research, Helps Families Cope with Loss